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Muscle and cardiac therapeutic strategies for Duchenne muscular dystrophy: past, present, and future

BACKGROUND: Duchenne muscular dystrophy (DMD) is a severe X-linked neuromuscular childhood disorder that causes progressive muscle weakness and degeneration and results in functional decline, loss of ambulation and early death of young men due to cardiac or respiratory failure. Although the major ca...

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Publicat a:Pharmacol Rep
Autors principals: Łoboda, Agnieszka, Dulak, Józef
Format: Artigo
Idioma:Inglês
Publicat: Springer International Publishing 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7550322/
https://ncbi.nlm.nih.gov/pubmed/32691346
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s43440-020-00134-x
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