Lanean...

Family Perspectives on Newborn Screening for X-Linked Adrenoleukodystrophy in California

X-linked adrenoleukodystrophy (ALD) is caused by gene variants in the ABCD1 gene, resulting in a varied clinical spectrum. Males with ALD present with symptoms ranging from isolated adrenal insufficiency and slowly progressive myelopathy to severe cerebral demyelination. Females who are heterozygous...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Int J Neonatal Screen
Egile Nagusiak: Schwan, Katharina, Youngblom, Janey, Weisiger, Kara, Kianmahd, Jessica, Waggoner, Rebecca, Fanos, Joanna
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: MDPI 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7510238/
https://ncbi.nlm.nih.gov/pubmed/33073000
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijns5040042
Etiketak: Etiketa erantsi
Etiketarik gabe, Izan zaitez lehena erregistro honi etiketa jartzen!