Real‐world effectiveness of eliglustat in treatment‐naïve and switch patients enrolled in the International Collaborative Gaucher Group Gaucher Registry

Eitemau Tebyg

• Clinical response to eliglustat in treatment-naïve patients with Gaucher disease type 1: Post-hoc comparison to imiglucerase-treated patients enrolled in the International Collaborative Gaucher Group Gaucher Registry
  gan: Jennifer Ibrahim, et al.
  Cyhoeddwyd: (2016-09-01)
• Clinical response to eliglustat in treatment-naïve patients with Gaucher disease type 1: Post-hoc comparison to imiglucerase-treated patients enrolled in the International Collaborative Gaucher Group Gaucher Registry
  gan: Ibrahim, Jennifer, et al.
  Cyhoeddwyd: (2016)
• Transformation in pretreatment manifestations of Gaucher disease type 1 during two decades of alglucerase/imiglucerase enzyme replacement therapy in the International Collaborative Gaucher Group (ICGG) Gaucher Registry
  gan: Mistry, Pramod K., et al.
  Cyhoeddwyd: (2017)
• Eliglustat substrate reduction therapy in children with Gaucher disease type 1
  gan: Noor Ul Ain, et al.
  Cyhoeddwyd: (2025-02-01)
• Outcomes after 18 months of eliglustat therapy in treatment‐naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trial
  gan: Mistry, Pramod K., et al.
  Cyhoeddwyd: (2017)