Refining clinical trial inclusion criteria to optimize the standardized response mean of the CMTPedS

The CMT Pediatric Scale (CMTPedS) is a reliable, valid, and responsive clinical outcome measure of disability in children with CMT. The aim of this study was to identify the most responsive patient subset(s), based on the standardized response mean (SRM), to optimize the CMTPedS as a primary outcome...

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Bibliographic Details
Published in:Ann Clin Transl Neurol
Main Authors: Cornett, Kayla M. D., Menezes, Manoj P., Bray, Paula, Shy, Rosemary R., Moroni, Isabella, Pagliano, Emanuela, Pareyson, Davide, Estilow, Tim, Yum, Sabrina W., Bhandari, Trupti, Muntoni, Francesco, Laura, Matilde, Reilly, Mary M., Finkel, Richard S., Eichinger, Katy J., Herrmann, David N., Shy, Michael E., Burns, Joshua
Format: Artigo
Language:Inglês
Published: John Wiley and Sons Inc. 2020
Subjects:
Brief Communications
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC7480902/
https://ncbi.nlm.nih.gov/pubmed/32762141
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/acn3.51145
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