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Precision Medicine for Lysosomal Disorders

Precision medicine (PM) is an emerging approach for disease treatment and prevention that accounts for the individual variability in the genes, environment, and lifestyle of each person. Lysosomal diseases (LDs) are a group of genetic metabolic disorders that include approximately 70 monogenic condi...

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Dades bibliogràfiques
Publicat a:Biomolecules
Autors principals: Pinto e Vairo, Filippo, Rojas Málaga, Diana, Kubaski, Francyne, Fischinger Moura de Souza, Carolina, de Oliveira Poswar, Fabiano, Baldo, Guilherme, Giugliani, Roberto
Format: Artigo
Idioma:Inglês
Publicat: MDPI 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7463721/
https://ncbi.nlm.nih.gov/pubmed/32722587
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/biom10081110
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