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Lysosomal Storage Disease-Associated Neuropathy: Targeting Stable Nucleic Acid Lipid Particle (SNALP)-Formulated siRNAs to the Brain as a Therapeutic Approach

More than two thirds of Lysosomal Storage Diseases (LSDs) present central nervous system involvement. Nevertheless, only one of the currently approved therapies has an impact on neuropathology. Therefore, alternative approaches are under development, either addressing the underlying enzymatic defect...

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Bibliografiske detaljer
Udgivet i:Int J Mol Sci
Main Authors: Coutinho, Maria Francisca, Santos, Juliana Inês, S. Mendonça, Liliana, Matos, Liliana, Prata, Maria João, S. Jurado, Amália, Pedroso de Lima, Maria C., Alves, Sandra
Format: Artigo
Sprog:Inglês
Udgivet: MDPI 2020
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7461213/
https://ncbi.nlm.nih.gov/pubmed/32785133
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21165732
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