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Phenotypic heterogeneity of neurofibromatosis type 1 in a large international registry

Neurofibromatosis type 1 (NF1) is a rare genetic disorder, characterized by the development of benign and malignant nerve tumors. Although all individuals with NF1 harbor genetic alterations in the same gene, the clinical manifestations of NF1 are extremely heterogeneous even among individuals who c...

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Pubblicato in:JCI Insight
Autori principali: Tabata, Mika M., Li, Shufeng, Knight, Pamela, Bakker, Annette, Sarin, Kavita Y.
Natura: Artigo
Lingua:Inglês
Pubblicazione: American Society for Clinical Investigation 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7455126/
https://ncbi.nlm.nih.gov/pubmed/32814709
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/jci.insight.136262
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