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Rapamycin and dexamethasone during pregnancy prevent tuberous sclerosis complex–associated cystic kidney disease
Chronic kidney disease is the main cause of mortality in patients with tuberous sclerosis complex (TSC) disease. The mechanisms underlying TSC cystic kidney disease remain unclear, with no available interventions to prevent cyst formation. Using targeted deletion of TSC1 in nephron progenitor cells,...
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Publié dans: | JCI Insight |
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Auteurs principaux: | , , , , |
Format: | Artigo |
Langue: | Inglês |
Publié: |
American Society for Clinical Investigation
2020
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Sujets: | |
Accès en ligne: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7406292/ https://ncbi.nlm.nih.gov/pubmed/32484794 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/jci.insight.136857 |
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