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Rapamycin and dexamethasone during pregnancy prevent tuberous sclerosis complex–associated cystic kidney disease

Chronic kidney disease is the main cause of mortality in patients with tuberous sclerosis complex (TSC) disease. The mechanisms underlying TSC cystic kidney disease remain unclear, with no available interventions to prevent cyst formation. Using targeted deletion of TSC1 in nephron progenitor cells,...

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Détails bibliographiques
Publié dans:JCI Insight
Auteurs principaux: Nechama, Morris, Makayes, Yaniv, Resnick, Elad, Meir, Karen, Volovelsky, Oded
Format: Artigo
Langue:Inglês
Publié: American Society for Clinical Investigation 2020
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7406292/
https://ncbi.nlm.nih.gov/pubmed/32484794
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/jci.insight.136857
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