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3-羟基异丁酰辅酶A水解酶缺乏症一例诊治体会并文献复习

A case of 3-hydroxyisobutyryl-CoA hydrolase deficiency was reported, and its clinical features, gene mutation characteristics, and diagnosis and treatment were analyzed with reference to related literature. The patient aged 1 year and 6 months had developmental regression and paroxysmal dystonia aft...

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Dades bibliogràfiques
Publicat a:Zhongguo Dang Dai Er Ke Za Zhi
Format: Artigo
Idioma:Inglês
Publicat: 中国当代儿科杂志编辑部 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7389760/
https://ncbi.nlm.nih.gov/pubmed/30111474
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.7499/j.issn.1008-8830.2018.08.009
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