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Phenotypic spectrum and genetic analysis in the fatal cases of Schaaf-Yang syndrome: Two case reports and literature review

RATIONALE: Schaaf-Yang syndrome, a rare imprinted hereditary disease caused by MAGEL2 variants, manifests as developmental delay/intellectual disability, neonatal hypotonia, feeding difficulties, contractures, and autism spectrum disorder. PATIENT CONCERNS: Patient 1 and 2 were infant girls presenti...

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Bibliografski detalji
Izdano u:Medicine (Baltimore)
Glavni autori: Chen, Xuefei, Ma, Xiaolu, Zou, Chaochun
Format: Artigo
Jezik:Inglês
Izdano: Wolters Kluwer Health 2020
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC7373511/
https://ncbi.nlm.nih.gov/pubmed/32702813
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MD.0000000000020574
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