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Gene therapy for global brain diseases: one small step for mice, one giant leap for humans
This scientific commentary refers to ‘Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy’, by Yoon et al. (doi:10.1093/brain/awaa161).
Guardat en:
| Publicat a: | Brain |
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| Autors principals: | , |
| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Oxford University Press
2020
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| Matèries: | |
| Accés en línia: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7364739/ https://ncbi.nlm.nih.gov/pubmed/32671401 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/brain/awaa189 |
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