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Gene therapy for global brain diseases: one small step for mice, one giant leap for humans

This scientific commentary refers to ‘Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy’, by Yoon et al. (doi:10.1093/brain/awaa161).

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Dades bibliogràfiques
Publicat a:Brain
Autors principals: Rahim, Ahad A, Gissen, Paul
Format: Artigo
Idioma:Inglês
Publicat: Oxford University Press 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7364739/
https://ncbi.nlm.nih.gov/pubmed/32671401
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/brain/awaa189
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