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Volanesorsen in the Treatment of Familial Chylomicronemia Syndrome or Hypertriglyceridaemia: Design, Development and Place in Therapy

Severe hypertriglyceridaemia is associated with pancreatitis and chronic pancreatitis-induced diabetes. Familial chylomicronaemia syndrome (FCS) is a rare autosomal recessive disorder of lipid metabolism characterised by high levels of triglycerides (TGs) due to failure of chylomicron clearance. It...

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Dades bibliogràfiques
Publicat a:Drug Des Devel Ther
Autors principals: Esan, Oluwayemisi, Wierzbicki, Anthony S
Format: Artigo
Idioma:Inglês
Publicat: Dove 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7351689/
https://ncbi.nlm.nih.gov/pubmed/32753844
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2147/DDDT.S224771
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