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Odevixibat and partial external biliary diversion showed equal improvement of cholestasis in a patient with progressive familial intrahepatic cholestasis

Untreated progressive familial intrahepatic cholestasis (PFIC) type 2, or bile salt exporter protein deficiency, frequently leads to severe pruritus, impaired growth and progressive liver fibrosis with risk of organ failure. We describe a 15-month-old male patient with severe pruritus diagnosed with...

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Pubblicato in:BMJ Case Rep
Autori principali: Slavetinsky, Christoph, Sturm, Ekkehard
Natura: Artigo
Lingua:Inglês
Pubblicazione: BMJ Publishing Group 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7326258/
https://ncbi.nlm.nih.gov/pubmed/32601135
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2019-234185
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