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Case Series of Creatine Deficiency Syndrome due to Guanidinoacetate Methyltransferase Deficiency

Guanidinoacetate methyltransferase (GAMT) deficiency is the second most common defect in the creatine metabolism pathway resulting in cerebral creatine deficiency syndrome (CCDS). We report three patients from two unrelated families, diagnosed with GAMT deficiency on next-generation sequencing. All...

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Dades bibliogràfiques
Publicat a:Ann Indian Acad Neurol
Autors principals: Narayan, Vinu, Mahay, Sunita Bijarnia, Verma, Ishwar Chander, Puri, Ratna Dua
Format: Artigo
Idioma:Inglês
Publicat: Wolters Kluwer - Medknow 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7313580/
https://ncbi.nlm.nih.gov/pubmed/32606525
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4103/aian.AIAN_367_18
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