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Emerging Approaches for Fluorescence-Based Newborn Screening of Mucopolysaccharidoses

Interest in newborn screening for mucopolysaccharidoses (MPS) is growing, due in part to ongoing efforts to develop new therapies for these disorders and new screening assays to identify increased risk for the individual MPSs on the basis of deficiency in the cognate enzyme. Existing tests for MPSs...

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Dettagli Bibliografici
Pubblicato in:Diagnostics (Basel)
Autori principali: Singh, Rajendra, Chopra, Shaileja, Graham, Carrie, Langer, Melissa, Ng, Rainer, Ullal, Anirudh J., Pamula, Vamsee K.
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI 2020
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7277946/
https://ncbi.nlm.nih.gov/pubmed/32403245
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/diagnostics10050294
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