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Cardiomyopathy and kidney function in agalsidase beta‐treated female Fabry patients: a pre‐treatment vs. post‐treatment analysis

AIMS: Long‐term treatment effect studies in large female Fabry patient groups are challenging to design because of phenotype heterogeneity and lack of appropriate comparison groups, and have not been reported. We compared long‐term cardiomyopathy and kidney function outcomes after agalsidase beta tr...

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Pubblicato in:ESC Heart Fail
Autori principali: Wanner, Christoph, Feldt‐Rasmussen, Ulla, Jovanovic, Ana, Linhart, Aleš, Yang, Meng, Ponce, Elvira, Brand, Eva, Germain, Dominique P., Hughes, Derralynn A., Jefferies, John L., Martins, Ana Maria, Nowak, Albina, Vujkovac, Bojan, Weidemann, Frank, West, Michael L., Ortiz, Alberto
Natura: Artigo
Lingua:Inglês
Pubblicazione: John Wiley and Sons Inc. 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7261571/
https://ncbi.nlm.nih.gov/pubmed/32100468
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ehf2.12647
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