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Correlation between ETFDH mutations and dysregulation of serum myomiRs in MADD patients

Multiple acyl-CoA dehydrogenase deficiency (MADD) is a rare fatty acids oxidation disorder which is often associated with deficiency of electron transfer flavoprotein dehydrogenase (ETFDH). In this study we reported clinical features and evaluation of expression profile of circulating muscle-specifi...

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Publicado en:Eur J Transl Myol
Autores principales: Missaglia, Sara, Pegoraro, Valentina, Marozzo, Roberta, Tavian, Daniela, Angelini, Corrado
Formato: Artigo
Lenguaje:Inglês
Publicado: PAGEPress Publications, Pavia, Italy 2020
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC7254427/
https://ncbi.nlm.nih.gov/pubmed/32499892
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4081/ejtm.2019.8880
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