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Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Ubiquitylation as a Novel Pharmaceutical Target for Cystic Fibrosis

Mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene decrease the structural stability and function of the CFTR protein, resulting in cystic fibrosis. Recently, the effect of CFTR-targeting combination therapy has dramatically increased, and it is expected that add-on dru...

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Detalhes bibliográficos
Publicado no:Pharmaceuticals (Basel)
Main Authors: Fukuda, Ryosuke, Okiyoneda, Tsukasa
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7243099/
https://ncbi.nlm.nih.gov/pubmed/32331485
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ph13040075
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