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Progress in Gene Therapy for Rhodopsin Autosomal Dominant Retinitis Pigmentosa

This brief review summarizes the major proof-of-concept gene therapy studies for autosomal dominant retinitis pigmentosa (RP) caused by mutations in the rhodopsin gene (RHO-adRP) that have been conducted over the past 20 years in various animal models. We have listed in tabular form the various appr...

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Detalles Bibliográficos
Publicado en:Adv Exp Med Biol
Autores principales: Sudharsan, Raghavi, Beltran, William A.
Formato: Artigo
Lenguaje:Inglês
Publicado: 2019
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC7217593/
https://ncbi.nlm.nih.gov/pubmed/31884598
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/978-3-030-27378-1_19
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