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Gene therapy for haemophilia

BACKGROUND: Haemophilia is a genetic disorder characterized by spontaneous or provoked, often uncontrolled, bleeding into joints, muscles and other soft tissues. Current methods of treatment are expensive, challenging and involve regular administration of clotting factors. Gene therapy for haemophil...

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Detalles Bibliográficos
Publicado en:Cochrane Database Syst Rev
Autores principales: Sharma, Akshay, Easow Mathew, Manu, Sriganesh, Vasumathi, Reiss, Ulrike M
Formato: Artigo
Lenguaje:Inglês
Publicado: John Wiley & Sons, Ltd 2020
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC7192367/
https://ncbi.nlm.nih.gov/pubmed/32342499
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/14651858.CD010822.pub4
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