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Improvement of MEFV gene variants classification to aid treatment decision making in familial Mediterranean fever

OBJECTIVE: FMF is an inherited autoinflammatory syndrome caused by mutations in the MEFV gene. MEFV variants are still largely classified as acvariant of uncertain significance, or with unresolved classification, posing significant challenges in FMF diagnosis. Rare Exome Variant Ensemble Learner (RE...

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Detalhes bibliográficos
Publicado no:Rheumatology (Oxford)
Main Authors: Accetturo, Matteo, D’Uggento, Angela Maria, Portincasa, Piero, Stella, Alessandro
Formato: Artigo
Idioma:Inglês
Publicado em: Oxford University Press 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7188344/
https://ncbi.nlm.nih.gov/pubmed/31411330
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/rheumatology/kez332
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