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Idebenone increases chance of stabilization/recovery of visual acuity in OPA1‐dominant optic atrophy

We previously documented that idebenone treatment in OPA1‐Dominant Optic Atrophy (OPA1‐DOA) led to some degrees of visual improvement in seven patients. We here present the results of a cohort study, which investigated the effect of off‐label idebenone administration in a larger OPA1‐DOA group compa...

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Detaylı Bibliyografya
Yayımlandı:Ann Clin Transl Neurol
Asıl Yazarlar: Romagnoli, Martina, La Morgia, Chiara, Carbonelli, Michele, Di Vito, Lidia, Amore, Giulia, Zenesini, Corrado, Cascavilla, Maria Lucia, Barboni, Piero, Carelli, Valerio
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: John Wiley and Sons Inc. 2020
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC7187718/
https://ncbi.nlm.nih.gov/pubmed/32243103
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/acn3.51026
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