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Pharmacological treatment for familial amyloid polyneuropathy

BACKGROUND: Disease‐modifying pharmacological agents for transthyretin (TTR)‐related familial amyloid polyneuropathy (FAP) have become available in the last decade, but evidence on their efficacy and safety is limited. This review focuses on disease‐modifying pharmacological treatment for TTR‐relate...

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Enregistré dans:
Détails bibliographiques
Publié dans:Cochrane Database Syst Rev
Auteurs principaux: Magrinelli, Francesca, Fabrizi, Gian Maria, Santoro, Lucio, Manganelli, Fiore, Zanette, Giampietro, Cavallaro, Tiziana, Tamburin, Stefano
Format: Artigo
Langue:Inglês
Publié: John Wiley & Sons, Ltd 2020
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7170468/
https://ncbi.nlm.nih.gov/pubmed/32311072
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/14651858.CD012395.pub2
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