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Pharmacological treatment for familial amyloid polyneuropathy

BACKGROUND: Disease‐modifying pharmacological agents for transthyretin (TTR)‐related familial amyloid polyneuropathy (FAP) have become available in the last decade, but evidence on their efficacy and safety is limited. This review focuses on disease‐modifying pharmacological treatment for TTR‐relate...

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Dettagli Bibliografici
Pubblicato in:Cochrane Database Syst Rev
Autori principali: Magrinelli, Francesca, Fabrizi, Gian Maria, Santoro, Lucio, Manganelli, Fiore, Zanette, Giampietro, Cavallaro, Tiziana, Tamburin, Stefano
Natura: Artigo
Lingua:Inglês
Pubblicazione: John Wiley & Sons, Ltd 2020
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7170468/
https://ncbi.nlm.nih.gov/pubmed/32311072
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/14651858.CD012395.pub2
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