A carregar...

The GALA project: practical recommendations for the use of migalastat in clinical practice on the basis of a structured survey among Italian experts

BACKGROUND: Oral migalastat has recently been approved for the treatment of Anderson-Fabry disease (FD) in patients aged ≥16 years with amenable mutations on the basis of two phase III trials, FACETS and ATTRACT. However, with the introduction of migalastat into clinical practice, it is important to...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Publicado no:Orphanet J Rare Dis
Main Authors: Chimenti, Cristina, Nencini, Patrizia, Pieruzzi, Federico, Feriozzi, Sandro, Mignani, Renzo, Pieroni, Maurizio, Pisani, Antonio
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7140546/
https://ncbi.nlm.nih.gov/pubmed/32264911
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-020-1318-8
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!