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Longitudinal serum biomarker screening identifies malate dehydrogenase 2 as candidate prognostic biomarker for Duchenne muscular dystrophy

BACKGROUND: Duchenne muscular dystrophy (DMD) is a fatal disease for which no cure is available. Clinical trials have shown to be largely underpowered due to inter‐individual variability and noisy outcome measures. The availability of biomarkers able to anticipate clinical benefit is highly needed t...

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Detalhes bibliográficos
Publicado no:J Cachexia Sarcopenia Muscle
Main Authors: Signorelli, Mirko, Ayoglu, Burcu, Johansson, Camilla, Lochmüller, Hanns, Straub, Volker, Muntoni, Francesco, Niks, Erik, Tsonaka, Roula, Persson, Anja, Aartsma‐Rus, Annemieke, Nilsson, Peter, Al‐Khalili Szigyarto, Cristina, Spitali, Pietro
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley and Sons Inc. 2019
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7113516/
https://ncbi.nlm.nih.gov/pubmed/31881125
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jcsm.12517
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