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Lysosomes as a therapeutic target

Lysosomes are membrane-bound organelles with roles in processes involved in degrading and recycling cellular waste, cellular signalling and energy metabolism. Defects in genes encoding lysosomal proteins cause lysosomal storage disorders, in which enzyme replacement therapy has proved successful. Gr...

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Pubblicato in:Nat Rev Drug Discov
Autori principali: Bonam, Srinivasa Reddy, Wang, Fengjuan, Muller, Sylviane
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group UK 2019
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7097195/
https://ncbi.nlm.nih.gov/pubmed/31477883
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41573-019-0036-1
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