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Genome editing technologies to treat rare liver diseases

Liver has a central role in protein and lipid metabolism, and diseases involving hepatocytes have often repercussions on multiple organs and systems. Hepatic disorders are frequently characterized by production of defective or non-functional proteins, and traditional gene therapy approaches have bee...

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Detalhes bibliográficos
Publicado no:Transl Gastroenterol Hepatol
Main Authors: Trevisan, Marta, Masi, Giulia, Palù, Giorgio
Formato: Artigo
Idioma:Inglês
Publicado em: AME Publishing Company 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7063531/
https://ncbi.nlm.nih.gov/pubmed/32258527
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.21037/tgh.2019.10.10
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