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Next-generation sequencing and recombinant expression characterized aberrant splicing mechanisms and provided correction strategies in factor VII deficiency

Despite the exhaustive screening of F7 gene exons and exon-intron boundaries and promoter region, a significant proportion of mutated alleles remains unidentified in patients with coagulation factor VII deficiency. Here, we applied next-generation sequencing to 13 FVII-deficient patients displaying...

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Detalhes bibliográficos
Publicado no:Haematologica
Main Authors: Ferraresi, Paolo, Balestra, Dario, Guittard, Caroline, Buthiau, Delphine, Pan-Petesh, Brigitte, Maestri, Iva, Farah, Roula, Pinotti, Mirko, Giansily-Blaizot, Muriel
Formato: Artigo
Idioma:Inglês
Publicado em: Ferrata Storti Foundation 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7049351/
https://ncbi.nlm.nih.gov/pubmed/31273093
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3324/haematol.2019.217539
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