Loading...

Genome Editing for Mucopolysaccharidoses

Genome editing holds the promise of one-off and potentially curative therapies for many patients with genetic diseases. This is especially true for patients affected by mucopolysaccharidoses as the disease pathophysiology is amenable to correction using multiple approaches. Ex vivo and in vivo genom...

Fuld beskrivelse

Na minha lista:
Bibliografiske detaljer
Udgivet i:Int J Mol Sci
Main Authors: Poletto, Edina, Baldo, Guilherme, Gomez-Ospina, Natalia
Format: Artigo
Sprog:Inglês
Udgivet: MDPI 2020
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7014411/
https://ncbi.nlm.nih.gov/pubmed/31941077
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21020500
Tags: Tilføj Tag
Ingen Tags, Vær først til at tagge denne postø!