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Novel Desmin Mutation Causing Myofibrillar Myopathy in a Hmong Family

Myofibrillar myopathies (MFM) are a clinically and genetically heterogenous group of inherited myopathies characterized by aggregation of Z-disc proteins. Mutations in desmin account for ~7% of MFM. We report here a Hmong family with an autosomal dominant MFM caused by a novel variant in the desmin...

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Detalles Bibliográficos
Publicado en:Front Neurol
Autores principales: Nicolau, Stefan, Howe, Benjamin M., Naddaf, Elie
Formato: Artigo
Lenguaje:Inglês
Publicado: Frontiers Media S.A. 2020
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6965354/
https://ncbi.nlm.nih.gov/pubmed/31998224
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fneur.2019.01375
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