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Mendelian disease caused by variants affecting recognition of Z-DNA and Z-RNA by the Zα domain of the double-stranded RNA editing enzyme ADAR

Variants in the human double-stranded RNA editing enzyme ADAR produce three well-characterized rare Mendelian Diseases: Dyschromatosis Symmetrica Hereditaria (OMIM: 127400), Aicardi-Goutières syndrome (OMIM: 615010) and Bilateral Striatal Necrosis/Dystonia. ADAR encodes p150 and p110 protein isoform...

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Detalhes bibliográficos
Publicado no:Eur J Hum Genet
Autor principal: Herbert, Alan
Formato: Artigo
Idioma:Inglês
Publicado em: Springer International Publishing 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6906422/
https://ncbi.nlm.nih.gov/pubmed/31320745
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41431-019-0458-6
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