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Endocrine and metabolic disorders in patients with Gaucher disease type 1: a review

BACKGROUND: Gaucher disease (GD) is one of the most prevalent lysosomal storage diseases and is associated with hormonal and metabolic abnormalities, including nutritional status disorders, hypermetabolic state with high resting energy expenditures, peripheral insulin resistance, hypoadiponectinaemi...

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Detalhes bibliográficos
Publicado no:Orphanet J Rare Dis
Main Authors: Kałużna, Małgorzata, Trzeciak, Isabella, Ziemnicka, Katarzyna, Machaczka, Maciej, Ruchała, Marek
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2019
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6889605/
https://ncbi.nlm.nih.gov/pubmed/31791361
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-019-1211-5
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