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Hematopoietic Stem Cell Transplantation for Severe Combined Immunodeficiency (SCID)

Severe Combined Immunodeficiencies (SCID) are a heterogeneous group of monogenetic diseases. We describe the typical clinical presentation of patients with SCID as well as basic principles in diagnosis and therapy by hematopoietic stem cell transplantation. Therapeutic strategies may differ between...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Front Pediatr
Egile Nagusiak: Haddad, Elie, Hoenig, Manfred
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Frontiers Media S.A. 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6877719/
https://ncbi.nlm.nih.gov/pubmed/31803700
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fped.2019.00481
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