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Clinical characteristics of individual organ system disease in non-motile ciliopathies

Non-motile ciliopathies (disorders of the primary cilia) include autosomal dominant and recessive polycystic kidney diseases, nephronophthisis, as well as multisystem disorders Joubert, Bardet-Biedl, Alström, Meckel-Gruber, oral-facial-digital syndromes, and Jeune chondrodysplasia and other skeletal...

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Dades bibliogràfiques
Publicat a:Transl Sci Rare Dis
Autors principals: Grochowsky, Angela, Gunay-Aygun, Meral
Format: Artigo
Idioma:Inglês
Publicat: IOS Press 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6864414/
https://ncbi.nlm.nih.gov/pubmed/31763176
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3233/TRD-190033
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