Laddar...

CRISPR for Neuromuscular Disorders: Gene Editing and Beyond

This is a review describing advances in CRISPR/Cas-mediated therapies for neuromuscular disorders (NMDs). We explore both CRISPR-mediated editing and dead Cas approaches as potential therapeutic strategies for multiple NMDs. Last, therapeutic considerations, including delivery and off-target effects...

Full beskrivning

Sparad:
Bibliografiska uppgifter
I publikationen:Physiology (Bethesda)
Huvudupphovsmän: Young, Courtney S., Pyle, April D., Spencer, Melissa J.
Materialtyp: Artigo
Språk:Inglês
Publicerad: American Physiological Society 2019
Ämnen:
Länkar:https://ncbi.nlm.nih.gov/pmc/articles/PMC6863376/
https://ncbi.nlm.nih.gov/pubmed/31389773
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1152/physiol.00012.2019
Taggar: Lägg till en tagg
Inga taggar, Lägg till första taggen!