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2396: Utility of the Modified Barium Swallow Impairment Profile as an outcome measure in oculopharyngeal muscular dystrophy

OBJECTIVES/SPECIFIC AIMS: Oculopharyngeal muscular dystrophy (OPMD) is a rare, late-onset muscular dystrophy that causes severe swallowing impairment (dysphagia). Although promising therapies are in the pipeline, validated dysphagia outcome measures for use in OPMD trials have not been established....

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Pubblicato in:J Clin Transl Sci
Autori principali: Youssof, Sarah, Romero-Clark, Carol
Natura: Artigo
Lingua:Inglês
Pubblicazione: Cambridge University Press 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6799303/
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1017/cts.2017.135
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