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A novel variant of the human mitochondrial DnaJ protein, Tid1, associates with a human disease exhibiting developmental delay and polyneuropathy

Here, we describe a single patient from a consanguineous family, who suffers from developmental delay, intellectual disability, hypermetropia, moderate alternating esotropia, unsteady gait, and peripheral polyneuropathy. Brain MRI revealed basal ganglia disease. Exome analysis disclosed a homozygous...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Eur J Hum Genet
Egile Nagusiak: Patra, Malay, Weiss, Celeste, Abu-Libdeh, Bassam, Ashhab, Motee, Abuzer, Shadi, Elpeleg, Orly, Mahajnah, Muhammad, Kessel, Amit, Azem, Abdussalam
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Springer International Publishing 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6777446/
https://ncbi.nlm.nih.gov/pubmed/30770860
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41431-019-0358-9
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