Φορτώνει......
Gene Therapy for Methylmalonic Acidemia: Past, Present, and Future
Methylmalonic acidemia (MMA) is a severe, and sometimes lethal, monogenic metabolic disorder in need of improved treatments. A number of new genomic therapies, which include canonical adeno-associated virus gene addition, genome editing, and systemic mRNA therapy, have shown great promise in murine...
Αποθηκεύτηκε σε:
| Τόπος έκδοσης: | Hum Gene Ther |
|---|---|
| Κύριοι συγγραφείς: | , |
| Μορφή: | Artigo |
| Γλώσσα: | Inglês |
| Έκδοση: |
Mary Ann Liebert, Inc., publishers
2019
|
| Θέματα: | |
| Διαθέσιμο Online: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6763959/ https://ncbi.nlm.nih.gov/pubmed/31303064 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2019.113 |
| Ετικέτες: |
Προσθήκη ετικέτας
Δεν υπάρχουν, Καταχωρήστε ετικέτα πρώτοι!
|