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Association between patient-reported outcomes and objective disease indices in people with NF2

OBJECTIVE: The association between patient-reported outcomes and currently used clinical trial endpoints, including total vestibular schwannoma (VS) volume and word recognition score (WRS) in neurofibromatosis type 2 (NF2), is not known. METHODS: A prospective observational study enrolling adult pat...

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Dettagli Bibliografici
Pubblicato in:Neurol Clin Pract
Autori principali: Shukla, Aishwarya, Hsu, Fang-Chi, Slobogean, Bronwyn, Langmead, Shannon, Lu, Yao, Blakeley, Jaishri O., Strowd, Roy E.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Lippincott Williams & Wilkins 2019
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6745746/
https://ncbi.nlm.nih.gov/pubmed/31583187
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/CPJ.0000000000000648
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