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The International Prospective Glanzmann Thrombasthenia Registry: Pediatric Treatment and Outcomes

Background  Standard treatment for Glanzmann thrombasthenia (GT), a severe inherited bleeding disorder, is platelet transfusion. Recombinant activated factor VII (rFVIIa) is reported to be effective in GT with platelet antibodies and/or refractoriness to platelet transfusions. Methods  We evaluated...

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Publicat a:TH Open
Autors principals: Zotz, Rainer B., Poon, Man-Chiu, Di Minno, Giovanni, D'Oiron, Roseline
Format: Artigo
Idioma:Inglês
Publicat: Georg Thieme Verlag KG 2019
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6742499/
https://ncbi.nlm.nih.gov/pubmed/31523745
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1055/s-0039-1696657
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