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Antisense Therapie Neurologischer Erkrankungen

There are few disease-modifying therapeutics for neurodegenerative diseases. Antisense oligonucleotide (ASO) therapeutics for spinal muscular atrophy, Duchenne muscular dystrophy, and transthyretin amyloidosis predict a robust future for ASOs in medicine. Perhaps the most significant advantage to AS...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Nervenarzt
Egile nagusia: Pulst, Stefan-M.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6730669/
https://ncbi.nlm.nih.gov/pubmed/31165208
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s00115-019-0724-4
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