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Analysis of the functional capacity outcome measures for myotonic dystrophy

OBJECTIVES: Defining clinically relevant outcome measures for myotonic dystrophy type 1 (DM1) that can be valid and feasible for different phenotypes has proven problematic. The Outcome Measures for Myotonic Dystrophy (OMMYD) group proposed a battery of functional outcomes: 6‐minute walk test, 30 se...

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Dades bibliogràfiques
Publicat a:Ann Clin Transl Neurol
Autors principals: Jimenez‐Moreno, Aura Cecilia, Nikolenko, Nikoletta, Kierkegaard, Marie, Blain, Alasdair P., Newman, Jane, Massey, Charlotte, Moat, Dionne, Sodhi, Jas, Atalaia, Antonio, Gorman, Grainne S., Turner, Chris, Lochmüller, Hanns
Format: Artigo
Idioma:Inglês
Publicat: John Wiley and Sons Inc. 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6689676/
https://ncbi.nlm.nih.gov/pubmed/31402614
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/acn3.50845
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