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Niemann-Pick Disease: An Approach for Diagnosis in Adulthood

Niemann-Pick (NP) disease is a rare, autosomal recessive disorder characterized by visceromegaly and neurological alterations due to the excessive storage of lipids, sphingomyelin, and cholesterol. It commonly affects the child population, and only 6% of it occurs in the adult population. Type A is...

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Detalles Bibliográficos
Publicado en:Cureus
Main Authors: Patiño-Escobar, Bonell, Solano, Maria H, Zarabanda, Laura, Casas, Claudia P, Castro, Carlos
Formato: Artigo
Idioma:Inglês
Publicado: Cureus 2019
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6663041/
https://ncbi.nlm.nih.gov/pubmed/31363448
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.7759/cureus.4767
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