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The migalastat GLP-HEK assay is the gold standard for determining amenability in patients with Fabry disease

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Bibliografske podrobnosti
izdano v:Mol Genet Metab Rep
Main Authors: Schiffmann, Raphael, Bichet, Daniel G., Benjamin, Elfrida, Wu, Xiaoyang, Giugliani, Roberto
Format: Artigo
Jezik:Inglês
Izdano: Elsevier 2019
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC6656697/
https://ncbi.nlm.nih.gov/pubmed/31367522
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2019.100494
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