Outcomes after 8 years of eliglustat therapy for Gaucher disease type 1: Final results from the Phase 2 trial

Lignende værker

• Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat
  af: Kamath, Ravi S., et al.
  Udgivet: (2014)
• Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials
  af: Lukina, Elena, et al.
  Udgivet: (2020)
• A phase 2 study of eliglustat tartrate (Genz-112638), an oral substrate reduction therapy for Gaucher disease type 1
  af: Lukina, Elena, et al.
  Udgivet: (2010)
• Improvement in hematological, visceral, and skeletal manifestations of Gaucher disease type 1 with oral eliglustat tartrate (Genz-112638) treatment: 2-year results of a phase 2 study
  af: Lukina, Elena, et al.
  Udgivet: (2010)
• Long-term adverse event profile from four completed trials of oral eliglustat in adults with Gaucher disease type 1
  af: Peterschmitt, M. Judith, et al.
  Udgivet: (2019)