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Clinical trials of disease-modifying agents in pediatric MS: Opportunities, challenges, and recommendations from the IPMSSG

OBJECTIVE: The impetus for this consensus discussion was to recommend clinical trial designs that can deliver high-quality data for effective therapies for pediatric patients, in a reasonable timeframe, with a key focus on short- and long-term safety. METHODS: The International Pediatric Multiple Sc...

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Detalhes bibliográficos
Publicado no:Neurology
Main Authors: Waubant, Emmanuelle, Banwell, Brenda, Wassmer, Evangeline, Sormani, Maria-Pia, Amato, Maria-Pia, Hintzen, Rogier, Krupp, Lauren, Rostásy, Kevin, Tenembaum, Silvia, Chitnis, Tanuja
Formato: Artigo
Idioma:Inglês
Publicado em: Lippincott Williams & Wilkins 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6556085/
https://ncbi.nlm.nih.gov/pubmed/31043474
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000007572
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