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Rubinstein–Taybi syndrome 2 with cerebellar abnormality and neural tube defect

Rubinstein–Taybi syndrome (RSTS) is a rare dominant disorder with intellectual disability, postnatal growth deficiency, and multiple congenital anomalies. Approximately 50–70% of the patients have a mutation in the CREBBP gene (RSTS1) and 5–10% display an EP300 gene mutation (RSTS2). Craniospinal ab...

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Dettagli Bibliografici
Pubblicato in:Clin Dysmorphol
Autori principali: Hadzsiev, Kinga, Gyorsok, Zsuzsanna, Till, Agnes, Czakó, Márta, Bartsch, Oliver
Natura: Artigo
Lingua:Inglês
Pubblicazione: Lippincott Williams & Wilkins 2019
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6553355/
https://ncbi.nlm.nih.gov/pubmed/30789376
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MCD.0000000000000262
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