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Novel mutation in TNPO3 causes congenital limb-girdle myopathy with slow progression

OBJECTIVE: We report a second family with autosomal dominant transportinopathy presenting with congenital or early-onset myopathy and slow progression, causing proximal and less pronounced distal muscle weakness. METHODS: Patients had clinical examinations, muscle MRI, EMG, and muscle biopsy studies...

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Bibliografski detalji
Izdano u:Neurol Genet
Glavni autori: Vihola, Anna, Palmio, Johanna, Danielsson, Olof, Penttilä, Sini, Louiselle, Daniel, Pittman, Sara, Weihl, Conrad, Udd, Bjarne
Format: Artigo
Jezik:Inglês
Izdano: Wolters Kluwer 2019
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC6515942/
https://ncbi.nlm.nih.gov/pubmed/31192305
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/NXG.0000000000000337
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