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Correlating Cystic Fibrosis Transmembrane Conductance Regulator Function with Clinical Features to Inform Precision Treatment of Cystic Fibrosis

Rationale: The advent of precision treatment for cystic fibrosis using small-molecule therapeutics has created a need to estimate potential clinical improvements attributable to increases in cystic fibrosis transmembrane conductance regulator (CFTR) function. Objectives: To derive CFTR function of a...

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Dades bibliogràfiques
Publicat a:Am J Respir Crit Care Med
Autors principals: McCague, Allison F., Raraigh, Karen S., Pellicore, Matthew J., Davis-Marcisak, Emily F., Evans, Taylor A., Han, Sangwoo T., Lu, Zhongzhou, Joynt, Anya T., Sharma, Neeraj, Castellani, Carlo, Collaco, Joseph M., Corey, Mary, Lewis, Michelle H., Penland, Chris M., Rommens, Johanna M., Stephenson, Anne L., Sosnay, Patrick R., Cutting, Garry R.
Format: Artigo
Idioma:Inglês
Publicat: American Thoracic Society 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6515867/
https://ncbi.nlm.nih.gov/pubmed/30888834
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1164/rccm.201901-0145OC
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