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Ataxia with Oculomotor Apraxia Type 4 with PNKP Common “Portuguese” and Novel Mutations in Two Belarusian Families

Ataxia with oculomotor apraxia type 4 (AOA4) is a rare autosomal recessive, PNKP -related disorder delineated in 2015 in Portugal. We diagnosed AOA4 by next generation sequencing (NGS) followed by Sanger's sequencing in three boys from two unrelated Belarusian families. In both families, one of...

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Detalhes bibliográficos
Publicado no:J Pediatr Genet
Main Authors: Rudenskaya, Galina E., Marakhonov, Andrey V., Shchagina, Olga A., Lozier, Ekaterina R., Dadali, Elena L., Akimova, Irina A., Petrova, Nika V., Konovalov, Fedor A.
Formato: Artigo
Idioma:Inglês
Publicado em: Georg Thieme Verlag KG 2019
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6499616/
https://ncbi.nlm.nih.gov/pubmed/31061747
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1055/s-0039-1684008
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